Two-year results of the ASCEND trial of olipudase alfa adults with chronic acid sphingomyelinase deficiency show parallel improvements in former placebo patients and further improvement in continuing olipudase alfa patients
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Dergi Başlığı
Dergi ISSN
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Yayıncı
Academic Press Inc Elsevier Science
Erişim Hakkı
info:eu-repo/semantics/closedAccess
Özet
[No abstract available]
Açıklama
18th Annual WORLD Symposium -- FEB 07-11, 2022 -- San Diego, CA
Anahtar Kelimeler
Kaynak
Molecular Genetics and Metabolism
WoS Q Değeri
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Cilt
135
Sayı
2










