One-year results of the placebo-controlled ASCEND trial of olipudase alfa enzyme replacement therapy in adults with chronic acid sphingomyelinase deficiency

dc.authorid0000-0002-4660-821X
dc.contributor.authorWasserstein, Melissa
dc.contributor.authorArash-Kaps, Laila
dc.contributor.authorBarbato, Antonio
dc.contributor.authorGallagher, Renata
dc.contributor.authorGiugliani, Roberto
dc.contributor.authorGuelbert, Norberto
dc.contributor.authorHollak, Carla
dc.date.accessioned2025-05-10T19:32:35Z
dc.date.issued2021
dc.departmentİstanbul Medeniyet Üniversitesi
dc.description.abstract[No abstract available]
dc.identifier.endpageS65
dc.identifier.issn1096-7192
dc.identifier.issn1096-7206
dc.identifier.scopusqualityQ2
dc.identifier.startpageS64
dc.identifier.urihttps://hdl.handle.net/20.500.14730/8314
dc.identifier.volume132
dc.identifier.wosWOS:000639219800092
dc.identifier.wosqualityQ2
dc.indekslendigikaynakWeb of Science
dc.language.isoen
dc.publisherAcademic Press Inc Elsevier Science
dc.relation.ispartofMolecular Genetics and Metabolism
dc.relation.publicationcategoryKonferans Öğesi - Uluslararası - Kurum Öğretim Elemanı
dc.rightsinfo:eu-repo/semantics/closedAccess
dc.snmzKA_WOS_20250302
dc.titleOne-year results of the placebo-controlled ASCEND trial of olipudase alfa enzyme replacement therapy in adults with chronic acid sphingomyelinase deficiency
dc.typeConference Object

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