One-year results of the placebo-controlled ASCEND trial of olipudase alfa enzyme replacement therapy in adults with chronic acid sphingomyelinase deficiency
| dc.authorid | 0000-0002-4660-821X | |
| dc.contributor.author | Wasserstein, Melissa | |
| dc.contributor.author | Arash-Kaps, Laila | |
| dc.contributor.author | Barbato, Antonio | |
| dc.contributor.author | Gallagher, Renata | |
| dc.contributor.author | Giugliani, Roberto | |
| dc.contributor.author | Guelbert, Norberto | |
| dc.contributor.author | Hollak, Carla | |
| dc.date.accessioned | 2025-05-10T19:32:35Z | |
| dc.date.issued | 2021 | |
| dc.department | İstanbul Medeniyet Üniversitesi | |
| dc.description.abstract | [No abstract available] | |
| dc.identifier.endpage | S65 | |
| dc.identifier.issn | 1096-7192 | |
| dc.identifier.issn | 1096-7206 | |
| dc.identifier.scopusquality | Q2 | |
| dc.identifier.startpage | S64 | |
| dc.identifier.uri | https://hdl.handle.net/20.500.14730/8314 | |
| dc.identifier.volume | 132 | |
| dc.identifier.wos | WOS:000639219800092 | |
| dc.identifier.wosquality | Q2 | |
| dc.indekslendigikaynak | Web of Science | |
| dc.language.iso | en | |
| dc.publisher | Academic Press Inc Elsevier Science | |
| dc.relation.ispartof | Molecular Genetics and Metabolism | |
| dc.relation.publicationcategory | Konferans Öğesi - Uluslararası - Kurum Öğretim Elemanı | |
| dc.rights | info:eu-repo/semantics/closedAccess | |
| dc.snmz | KA_WOS_20250302 | |
| dc.title | One-year results of the placebo-controlled ASCEND trial of olipudase alfa enzyme replacement therapy in adults with chronic acid sphingomyelinase deficiency | |
| dc.type | Conference Object |










