Adults with chronic acid sphingomyelinase deficiency show significant visceral, pulmonary, and hematologic improvements after enzyme replacement therapy with olipudase-alfa: 1-year results of the ASCEND placebo-controlled trial
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Academic Press Inc Elsevier Science
Erişim Hakkı
info:eu-repo/semantics/closedAccess
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[No abstract available]
Açıklama
17th Annual Research Meeting of the We're-Organizing-Research-for-Lysosomal-Diseases-Symposium (WORLDSymposium) -- FEB 07-12, 2021 -- ELECTR NETWORK
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Molecular Genetics and Metabolism
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132
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2
